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Clinical Trials

Search among the pediatric clinical trials we have open at the Vall d'Hebron Research Institute.

Disease Medication Phase Recruitment Information
Ulcerative Colitis Upadacitinib Phase III Yes More info
Acute Myeloid Leukemia (Pediatric 0-18 years) NOPHO-DBH AML 2012 Protocol Phase III No More info
Adolescent Renal Allografts Belatacept-based Immunosuppressive Regimen Phase III No More info
Ataxia Telangiectasia EryDex Phase III No More info
Atrofia muscular espinal Nusinersen (BIIB058) Phase II No More info
Biliary Atresia Odevixibat (A4250) Phase III No More info
Células Falciformes con crisis vaso-oclusivas. Crizanlizumab, with or without Hydroxyurea/Hydroxycarbamide Phase II No More info
Classic Congenital Adrenal Hyperplasia (CAH) Crinecerfont (NBI-74788) Phase III No More info
Deficiencia de timidina quinasa 2 Combination pyrimidine nucleos(t)ides Phase II No More info
Distrofia muscular de Duchenne PF-06939926 Phase III No More info
Dravet and Lennox-Gastaut Syndromes Soticlestat Phase III No More info
Dravet syndrome or Lennox-Gastaut syndrome ZX008 (Fenfluramine Hydrochloride) Phase III No More info
Duchenne muscular dystrophy DYNE-251 Phase II No More info
Enfermedad Pulmonar Intersticial Nintedanib Phase III No More info
Epilepsia relacionada con CET Ganaxolone (GNX) Phase III No More info
Glomerulopatía C3 primaria o glomerulonefritis membranoproliferativa mediada por inmunocomplejos Pegcetacoplan Phase III No More info
Haemophilia A Recombinant Coagulation Factor VIII Fc-von Willebrand Factor-XTEN Fusion Protein (rFVIIIFc-VWF-XTEN; BIVV001) Phase III No More info
Hemofilia A con inhibidores NNC0365-3769 (Mim8) Phase III No More info
Hepatoblastoma y carcinoma hepatocelular C5VD, SIOPEL-3 high risk, cisplatin monotherapy, GEMOX Phase III No More info
Hereditary Angioedema Type I or II KVD900 (oral Plasma Kallikrein Inhibitor) Phase III No More info
Hiperoxaluria Primaria Nedosiran Phase II No More info
Hipotensión resistente a las catecolaminas asociada a shock distributivo LJPC-501 Phase II No More info
Hypoglycemia associated with congenital hyperinsulinism RZ358 Phase III No More info
Immune Thrombocytopenia (ITP) Rilzabrutinib (PRN1008) Phase III No More info