A 2-Part, Randomized, Double-Blind, Placebo-Controlled Study in Participants with Duchenne Muscular Dystrophy Amenable to Exon 4

A 2-Part, Randomized, Double-Blind, Placebo-Controlled Study in Participants with Duchenne Muscular Dystrophy Amenable to Exon 45 Skipping with an Initial Multiple Ascending Dose Part A to Assess the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of ENTR-601-45, Followed by Part B to Evaluate the Safety and Efficacy of ENTR-601-45

Obert

Codi protocol: ENTR-601-45-201
Codi EudraCT: _
Grup de recerca: Teràpies i Innovació en Neuropediatria i altres malalties rares pediàtriques
Servei: Pediatria General i Especialitats
Investigador/a principal: Gómez Andrés, David
Malaltia: Malalties del sistema nerviós
Fase: Fase I